THE TURNER SYNDROME LONG-TERM COMORBIDITIES STUDY

  • Research type

    Research Study

  • Full title

    Long-term observational study of women with Turner Syndrome and factors leading to associated co-morbidities including metabolic, cardiac, fertility, hormonal and bone parameters

  • IRAS ID

    249842

  • Contact name

    Helen Turner

  • Contact email

    helen.turner@ouh.nhs.uk

  • Sponsor organisation

    Oxford University Hospitals NHS Foundation Trust

  • Duration of Study in the UK

    10 years, 0 months, 1 days

  • Research summary

    Turner syndrome (TS) is the most common sex-chromosome disorder in females, affecting 1:2000 live-born girls. It is caused by the loss of an entire X chromosome, loss of a portion of the X, or complex rearrangements affecting the X chromosome. Structural abnormalities can include deletions of the short or long arms of the X chromosome, duplications (isochromosomes), or ring chromosomes. Some individuals are mosaic and carry one or more additional cell lines. There is a highly variable clinical spectrum. TS patients with a 45,X karyotype tend to have more clinical features than those who are mosaic with a normal cell line. The typical features of TS are short stature and ovarian failure. Congenital cardiovascular anomalies occur in approximately 50%, including bicuspid aortic valve, aortic coarctation, elongated transverse aortic arch and partial anomalous pulmonary venous connection. Women with TS have an increased risk for aortic dilatation and aortic dissection. Many women with TS have auto-immune disorders, osteoporosis and associated metabolic risk factors. Liver enzymes are often raised and steatosis is frequent; also, a 5-fold increase in the risk of cirrhosis has been reported.
    Risk assessment in TS is compromised by insufficient insight into the prevalence and causes of different syndrome-associated traits that may impact adversely on prognosis. This is especially the case for cardiovascular contributions to the excess all-cause mortality, where congenital and acquired heart disease contribute to up to 50% of all-cause mortality.
    We plan an observational study on karyotypically proven TS, followed in the adult TS clinic in OCDEM-Oxford University Hospitals. Data on TS women will be collected retrospectively and prospectively. Standard routine care - guidelines based - will be followed. The aim of the study is to extend the established karyotype-phenotype and to provide a better understanding of the causation and long term course of the TS related comorbidities.

  • REC name

    West Midlands - Solihull Research Ethics Committee

  • REC reference

    19/WM/0159

  • Date of REC Opinion

    22 May 2019

  • REC opinion

    Further Information Favourable Opinion