Proteomics and iPSC generation in NF1 autism

  • Research type

    Research Study

  • Full title

    PILOT PROTEOMIC STUDY & PLURIPOTENT STEM CELL GENERATION IN NEUROFIBROMATOSIS TYPE 1 AUTISM

  • IRAS ID

    246779

  • Contact name

    Shruti Garg

  • Contact email

    shruti.garg@manchester.ac.uk

  • Sponsor organisation

    University of Manchester

  • Duration of Study in the UK

    3 years, 6 months, 28 days

  • Research summary

    Neurofibromatosis type 1(NF1) is a common genetic disorder affecting 1 in 2500 people. About 25% of children with NF1 are also affected by Autism Spectrum Disorder (ASD). We don't understand why some children are affected by autism whilst other are not. The aims of this study are: (1) whether we can develop a blood test that can be used to identify autism (2) to develop stem cells from blood taken from children with NF1 autism. These stem cells can be used to understand more about brain development in children with NF1 and autism.

  • REC name

    East of England - Cambridgeshire and Hertfordshire Research Ethics Committee

  • REC reference

    18/EE/0250

  • Date of REC Opinion

    24 Jul 2018

  • REC opinion

    Favourable Opinion