Phase 2 Study to Evaluate the Safety and Efficacy of Pegcetacoplan

  • Research type

    Research Study

  • Full title

    An Open-Label, Randomized, Controlled, Phase 2 Study to Evaluate the Safety and Efficacy of Pegcetacoplan in the Treatment of Post Transplant Recurrence of C3G or IC-MPGN

  • IRAS ID

    286210

  • Contact name

    David Kavanagh

  • Contact email

    David.Kavanagh@newcastle.ac.uk

  • Sponsor organisation

    Apellis Pharmaceuticals, Inc.

  • Eudract number

    2020-002637-15

  • Clinicaltrials.gov Identifier

    IND: 136409, Regulatory Agency Identifier Number(s)

  • Duration of Study in the UK

    1 years, 10 months, 1 days

  • Research summary

    Two similar diseases, complement component 3 glomerulopathy (C3G) and immune complex
    membranoproliferative glomerulonephritis (IC-MPGN), will be studied in this clinical trial. C3 refers to a blood protein and the 'G' refers to glomerulopathy, meaning damage to the part of the kidney that filters blood, called glomeruli, in the kidney] and IC-MPGN (glomerulonephritis is a group of diseases that injure the glomeruli) are rare, chronic diseases that are a result of over-activation of part of the immune system. This system is called the complement system. When the complement system is not well controlled, this can result in damage to the glomerulus, a network of small blood vessels in the kidney, which filters (cleans) the blood. Over time, this stops the kidneys from removing waste in the blood. This waste, if not removed from the blood, builds up in the body and may lead to kidney failure.
    Pegcetacoplan (APL-2) is being studied in this clinical trial and works by turning down the complement system, a part of your immune system that is over-activated in people with C3G or IC-MPGN, and causing damage to the kidneys. Under normal conditions, the complement system will help remove pathogens and damaged cells without hurting the body. However, sometimes uncontrolled or improper activation of the complement system can damage the body.
    Up to 12 adults who have been diagnosed with post-transplant recurrence of C3G or IC MPGN will be enrolled in this study across 25 study centers globally.
    The participation in this study could last up to 84 weeks (approximately 1 year and 8 months) and include at least 22 study clinic visits. After completion of the 52-week (1 year) treatment period the patient may be offered to enter into an open-label extension study.

  • REC name

    North East - Newcastle & North Tyneside 2 Research Ethics Committee

  • REC reference

    20/NE/0283

  • Date of REC Opinion

    22 Dec 2020

  • REC opinion

    Favourable Opinion