HGT-1410 in Pediatric Patients with Early Stage MPS IIIA
Research type
Research Study
Full title
A Randomized, Controlled, Open-label, Multicenter, Phase IIb Safety and Efficacy Study of HGT-1410 (Recombinant Human Heparan N Sulfatase) Administration via an Intrathecal Drug Delivery Device in Pediatric Patients with Early Stage Mucopolysaccharidosis Type III A Disease
IRAS ID
137186
Contact name
Maureen Cleary
Contact email
Sponsor organisation
Shire Human Genetic Therapies, Inc.
Eudract number
2013-003450-24
REC name
London - West London & GTAC Research Ethics Committee
REC reference
13/LO/1694
Date of REC Opinion
23 Dec 2013
REC opinion
Further Information Favourable Opinion