Gene Therapy for WAS follow-up, version 1.0
Research type
Research Study
Full title
LONG TERM SAFETY FOLLOW UP OF PATIENTS ENROLLED IN THE PHASE I/II CLINICAL TRIAL OF HAEMATOPOIETIC STEM CELL GENE THERAPY FOR THE WISKOTT-ALDRICH SYNDROME(GTG 002-07 AND GTG 003-08)
IRAS ID
148367
Contact name
Adrian Thrasher
Contact email
Sponsor organisation
Genethon
Eudract number
2014-000274-20
REC name
London - West London & GTAC Research Ethics Committee
REC reference
14/LO/0395
Date of REC Opinion
14 May 2014
REC opinion
Further Information Favourable Opinion