DCM SUPPORT Study

  • Research type

    Research Study

  • Full title

    PHASE II STUDY ASSESSING THE COMBINED USE OF AUTOLOGOUS BONE MARROW DERIVED MONONUCLEAR CELLS AND G-CSF WITH PERCUTANEOUS CIRCULATORY ASSISTANCE IN THE TREATMENT OF DILATED CARDIOMYOPATHY

  • IRAS ID

    224790

  • Contact name

    Anthony Mathur

  • Contact email

    a.mathur@qmul.ac.uk

  • Sponsor organisation

    Queen Mary Innovation Centre, Queen Mary University of London

  • Eudract number

    2018-001063-23

  • ISRCTN Number

    ISRCTN00000000

  • Clinicaltrials.gov Identifier

    NCT00000000

  • Duration of Study in the UK

    3 years, 0 months, 1 days

  • Research summary

    Dilated cardiomyopathy (DCM) is the leading cause of heart failure in younger patients and is the most common indication for cardiac transplantation. Although a proportion of DCM patients recover heart function, the majority suffer a progressive decline in left ventricular ejection fraction (LVEF – pumping performance of the main chamber in the heart) with high levels of morbidity and mortality.

    The REGENERATE-DCM trial yielded encouraging results with an improvement in LVEF and symptoms for participants compared to placebo. This trial utilised bone marrow derived mononuclear cells (BMMNC) following 5 days of G-CSF administration (a hormone that stimulates bone marrow to make more cells) and ultimately these cells were infused down the coronary arteries of participants (intracoronary infusion). This trial looked at patients with moderate LVEF (35-45%). Patients with severely impaired LVEF (≤35%) have been excluded from clinical trials even though it is likely they would derive most benefit. We therefore propose the DCM SUPPORT Study where intracoronary infusion of BMMNC and adjunctive G-CSF will be utilised in a patient population with DCM and LVEF ≤30%. A mechanical pump will also be utilised to provide peri-procedural blood pressure support during the infusion of BMMNC and improve procedural safety. This device helps the patient’s heart pump blood around the body.

    The DCM SUPPORT study is a single centre, single arm, phase II pilot study. The primary endpoint will be a change in LVEF from baseline measured by a CT scan of the heart at 3 months. The secondary endpoints include change in LVEF from baseline measured by a CT scan of the heart at 12 months, in-hospital procedural related morbidity / mortality and assessment of major adverse cardiac events (MACE; death, heart attack, need for repeat heart revascularisation), change in exercise capacity and NYHA class at 3 months and 12 months respectively. The NYHA classification is a quantitative way of assessing a patient’s heart failure symptoms. It places patients into one of four categories (I – IV).

  • REC name

    South Central - Oxford A Research Ethics Committee

  • REC reference

    18/SC/0195

  • Date of REC Opinion

    14 Jun 2018

  • REC opinion

    Further Information Favourable Opinion