Avacopan in Patients with C3 Glomerulopathy

  • Research type

    Research Study

  • Full title

    A Randomized, Double-Blind, Placebo-Controlled Phase 2 Study to Evaluate the Safety and Efficacy of Avacopan (CCX168) in Patients with C3 Glomerulopathy

  • IRAS ID

    234786

  • Contact name

    David Kavanagh

  • Contact email

    david.kavanagh@ncl.ac.uk

  • Sponsor organisation

    ChemoCentryx, Inc.

  • Eudract number

    2017-001821-42

  • Duration of Study in the UK

    2 years, 2 months, 0 days

  • Research summary

    Summary of Research

    Avacopan is an investigational medicinal product being developed by ChemoCentryx, Inc. and is being studied for the treatment of a certain type of vasculitis, called ANCA-Associated Vasculitis (AAV).
    In C3 glomerulopathy, part of the immune system is not regulated appropriately. This leads to over-activation of the system, resulting in deposition of complement products in the filtration units of the kidney. One way to treat C3 glomerulopathy may be to regulate the action of a specific protein that is part of the complement system called C5a on its receptor. Avacopan is a medicinal product that directly targets this receptor and blocks the activity of C5a. Patients with C3G often have progressive deterioration in kidney function, ultimately leading to end-stage kidney disease.
    Currently, there is no approved treatment for patients with C3 glomerulopathy. Immunosuppressive drugs such as cyclophosphamide, mycophenolate mofetil, and glucocorticoids, as well as biologics have been used with limited success. Avacopan is in Phase 3 clinical development for treatment of patients with anti-neutrophil cytoplasmic AAV. Phase 2 study data with avacopan in patients with AAV indicate effectiveness with avacopan given twice daily, based on improvement in disease activity, a significant anti- proteinuric effect (reduction of protein in the urine), and improvement in quality of life among other improved disease parameters. This treatment effect was observed in subjects receiving avacopan plus cyclophosphamide or rituximab, but with no oral glucocorticoids. This provides support for testing drugs that targets the C5a receptor, such as avacopan.
    This study is being done to evaluate the effect and safety of avacopan on kidney disease activity in subjects with C3 glomerulopathy compared with a placebo for the first part of the study. This study will also assess the safety of avacopan. Safety is based on physical examinations, the side effects and safety laboratory changes over the course of the study.

    Summary of Results

    https://www.clinicaltrials.gov/ct2/show/NCT03301467?term=CL011_168&draw=2&rank=1

  • REC name

    North East - Newcastle & North Tyneside 1 Research Ethics Committee

  • REC reference

    18/NE/0052

  • Date of REC Opinion

    24 Apr 2018

  • REC opinion

    Further Information Favourable Opinion